Authors: Charles Peters, M.D., Virginie Bonnamain, Ph.D. and Stephan Kemp, Ph.D. What is hematopoietic stem cell transplantation? Hematopoietic stem cell... [...]
Gene Therapy for ALD
Authors: Virginie Bonnamain, Ph.D. and Stephan Kemp, Ph.D. In 2009, Drs. Nathalie Cartier and Patrick Aubourg and colleagues (Saint Vincent... [...]
Lorenzo’s oil
Gerald Raymond, M.D., Marc Engelen M.D., Ph.D. and Stephan Kemp Ph.D. VLCFA restricted diet The biochemical abnormality of ALD was... [...]
Lovastatin in ALD
Marc Engelen, M.D., Ph.D. & Stephan Kemp, Ph.D. New England Journal of Medicine 2010 Jan 21;362(3):276-277. In 1999, it was... [...]
Adrenal insufficiency
Authors: Gabor Linthorst, M.D., Ph.D. and Stephan Kemp, Ph.D. Males Adrenal insufficiency (or Addison’s disease) is common in ALD: The... [...]
The adrenal gland
Gabor Linthorst, M.D., Ph.D. and Stephan Kemp, Ph.D. Adrenal anatomy The adrenal glands are small triangular organs located above the... [...]
Lorenzo Odone
Lorenzo Odone has died from pneumonia aged 30. (May 29, 1978 – May 30, 2008) Lorenzo Odone, whose parents’ battle... [...]
Treatment options
This section includes pages about treatment options for adrenoleukodystrophy, adrenal insufficiency, hematopoietic stem cell transplantation, gene therapy, etc. [...]
