Treatment options

Hematopoietic stem cell transplantation

Charles Peters, M.D. and Stephan Kemp, Ph.D. This section of the website will focus primarily on childhood-onset cerebral ALD which... [...]

Gene Therapy for ALD

Stephan Kemp, Ph.D. In 2009, Drs. Nathalie Cartier and Patrick Aubourg and colleagues (Saint Vincent de Paul Hospital, Paris, France)... [...]

Lorenzo’s oil

Gerald Raymond, M.D., Marc Engelen M.D., Ph.D. and Stephan Kemp Ph.D. VLCFA restricted diet The biochemical abnormality of ALD was... [...]

Lovastatin in ALD

Marc Engelen, M.D., Ph.D. & Stephan Kemp, Ph.D. New England Journal of Medicine 2010 Jan 21;362(3):276-277. It 1999, it was... [...]

Adrenal insufficiency

Gabor Linthorst, M.D., Ph.D. and Stephan Kemp, Ph.D. Males Adrenal insufficiency is seen often in ALD. The vast majority (80%... [...]

The adrenal gland

Gabor Linthorst, M.D., Ph.D. and Stephan Kemp, Ph.D. Anatomy Adrenal glands are small triangular organs located on top of the... [...]

Lorenzo Odone

Lorenzo Odone has died from pneumonia aged 30. (May 29, 1978 – May 30, 2008) Lorenzo Odone, whose parents’ battle... [...]

Treatment options

Read about successful and unsuccessful treatment options. [...]